In the field of gene transfer medicine, a range of vectors that have different properties might be used. On top of the intrinsic vector features, transgene and expression cassette characteristics as ...
Duchenne muscular dystrophy (DMD) is an X-linked, lethal disorder of skeletal muscle caused by a defect in the dystrophin gene, which encodes a large sub-sarcolemmal cytoskeletal protein. The absence ...
Nanoparticles can be used in gene therapy to transfer therapeutic genes in to brain cells and helps in studying genetic mechanism of brain diseases. Nanoparticles can be used in gene therapy to ...